Duchenne Muscular Dystrophy (DMD) Drugs Market Size, Share & Trends Analysis Report By Therapeutic Approach (Mutation Suppression, Exon Skipping, Steroid Therapy) And Segment Forecasts, 2018 - 2023

Table of Contents

Chapter 1 Research Methodology
                  1.1 Information Procurement
                  1.2 Information or Data Analysis
                      1.2.1 Market formulation & validation
Chapter 2 Executive Summary
Chapter 3 Disease Primer and Epidemiology
                  3.1 Disease Primer
                      3.1.1 Symptoms
                      3.1.2 Progression of Disease
                  3.2 Epidemiology
                  3.3 Current Prevalence and Incidence of Seven Major Markets (U.S., Japan, EU5)
                  3.4 Forecast Prevalence and Incidence for Seven Major Markets (U.S., Japan, EU5)
Chapter 4 Global Duchenne Muscular Dystrophy Drugs Market Overview
                  4.1 Introduction and Market Overview
                      4.1.1 Segmentation, by therapeutic approach
                          4.1.1.1 Mutation suppression
                          4.1.1.2 Exon skipping
                          4.1.1.3 Steroid therapy
                      4.1.2 Segmentation, by major markets
                          4.1.2.1 U.S.
                          4.1.2.2 EU5
                          4.1.2.3 Japan
                      4.1.3 Market size and forecast
                      4.1.4 Sales performance
                      4.1.5 Market share distribution
                      4.1.6 Market dynamics among leading brands
                  4.2 Drivers and Challenges
                  4.3 Deals Landscape (2013-2018)
                  4.4 Pricing and Reimbursement
                  4.5 SWOT Analysis
Chapter 5 Duchenne Muscular Dystrophy Drugs Market: Pipeline Intelligence
                  5.1 Pipeline Landscape
                      5.1.1 Drugs in development
                      5.1.2 Key R&D trends
                          5.1.2.1 Corticosteroids
                          5.1.2.2 NF-κB Inhibitor
                          5.1.2.3 Anti-myostatin
                          5.1.2.4 Gene Therapy
                          5.1.2.5 Exon Skipping Platform
                  5.2 Late-Stage Pipeline
                  5.3 Profile of Disruptive Drugs
                      5.3.1 Vamorolone (VBP15)
                      5.3.2 SMT-C1100 (ezutromid)
                      5.3.3 CAT-1004 (Edasalonexent)
                      5.3.4 WVE-210201
                      5.3.5 AAV1-FS344
Chapter 6 Company Profiles
                  6.1 Sarepta Therapeutics
                      6.1.1 Company overview
                      6.1.2 Current product portfolio
                      6.1.3 Product forecast sales up to 2023
                      6.1.4 Company - key news flow
                      6.1.5 Pipeline view
                      6.1.6 Pipeline forecast
                      6.1.7 Catalysts and event calendar
                      6.1.8 SWOT analysis
                  6.2 PTC Therapeutics
                      6.2.1 Company overview
                      6.2.2 Current product portfolio
                      6.2.3 Product forecast sales up to 2023
                      6.2.4 Company - key news flow
                      6.2.5 Pipeline view
                      6.2.6 Pipeline forecast
                      6.2.7 Catalysts and event calendar
                      6.2.8 SWOT Analysis
                  6.3 Santhera Pharmaceuticals
                      6.3.1 Company overview
                      6.3.2 Current product portfolio
                      6.3.3 Product forecast sales up to 2023
                      6.3.4 Company - key news flow
                      6.3.5 Pipeline view
                      6.3.6 Pipeline forecast
                      6.3.7 Catalysts and event calendar
                      6.3.8 SWOT analysis
                  6.4 Italfarmaco
                      6.4.1 Company overview
                      6.4.2 Current product portfolio
                      6.4.3 Company - key news flow
                      6.4.4 Pipeline view
                      6.4.5 Pipeline forecast
                      6.4.6 Catalysts and event calendar
                      6.4.7 SWOT analysis
                  6.5 Catabasis
                      6.5.1 Company overview
                      6.5.2 Current product portfolio
                      6.5.3 Company - key news flow
                      6.5.4 Pipeline view
                      6.5.5 Pipeline forecast
                      6.5.6 Catalysts and event calendar
                      6.5.7 SWOT analysis
Chapter 7 Market Outlook
                  7.1 What the Future Holds
                  7.2 Winners and Losers
                  7.3 Emerging Companies
                  7.4 The Road Ahead

List of Tables

TABLE 1 Duchenne Muscular Dystrophy Prevalence and Incidence - 2017
TABLE 2 Forecast Duchenne Muscular Dystrophy Prevalence and Incidence, 2017 - 2023
TABLE 3 Duchenne Muscular Dystrophy Drugs Market Size and Forecast (in USD million)
TABLE 4 Geographic Sales Performance, by Seven Major Markets (in USD million)
TABLE 5 Duchenne Muscular Dystrophy Drugs Market, by Therapeutic Approach (in USD million)
TABLE 6 Sales Forecast of Approved Treatments (in USD million)
TABLE 7 Duchenne Muscular Drugs Sales Forecast, by Company (in USD million)
TABLE 8 Duchenne Muscular Dystrophy Drugs Market Share, by Company (in USD million)
TABLE 9 Duchenne Muscular Dystrophy Deals Landscape (2013 - 2018)
TABLE 10 Duchenne Muscular Dystrophy Drugs in Development
TABLE 11 Late-Stage Duchenne Muscular Dystrophy Pipeline
TABLE 12 Pipeline Forecast - Global Duchenne Muscular Drugs Market
TABLE 13 Profile of Disruptive Drug: Vamorolone (VBP15)
TABLE 14 Profile of Disruptive Drug: SMT-C1100 (ezutromid)
TABLE 15 Profile of Disruptive Drug: CAT-1004 (edasalonexent)
TABLE 16 Profile of Disruptive Drug: WVE-210201
TABLE 17 Profile of Disruptive Drug: AAV1-FS344
TABLE 18 Product Portfolio: Exondys 51
TABLE 19 Exondys 51 Sales Forecast through 2023
TABLE 20 Sarepta Pipeline View
TABLE 21 Sarepta - Upcoming Events and Catalysts
TABLE 22 Product Portfolio: Translarna
TABLE 23 Product Portfolio: Emflaza
TABLE 24 Translarna Sales Forecast through 2023
TABLE 25 Emflaza Sales Forecast through 2023
TABLE 26 PTC Pipeline View
TABLE 27 PTC - Upcoming Events and Catalysts
TABLE 28 Product Portfolio: Raxone
TABLE 29 Raxone Sales Forecast through 2023
TABLE 30 Santhera Pipeline View
TABLE 31 Santhera - Upcoming Events and Catalysts
TABLE 32 Product Portfolio: Givinostat
TABLE 33 Italfarmaco Pipeline View
TABLE 34 Italfarmaco - Upcoming Events and Catalysts
TABLE 35 Product Portfolio: CAT-1004
TABLE 36 Catabasis Pipeline View
TABLE 37 Catabasis - Upcoming Events and Catalysts

List of Figures

FIG. 1 Market Research Process
FIG. 2 Information Procurement
FIG. 3 Primary Research Pattern
FIG. 4 Market Research Approaches
FIG. 5 Value Chain Based Sizing & Forecasting
FIG. 6 QFD Modeling for Market Share Assessment
FIG. 7 Progression of Duchenne Muscular Dystrophy
FIG. 8 Current Prevalence Across Seven Major Markets - 2017
FIG. 9 Current Incidence Across Seven Major Markets - 2017
FIG. 10 Market segmentation & scope
FIG. 11 Geographic Sales Performance, by Seven Major Markets 2017
FIG. 12 Duchenne Muscular Dystrophy Drugs Market, by Therapeutic Approach
FIG. 13 Duchenne Muscular Dystrophy Sales Trend, by Therapeutic Approach
FIG. 14 Duchenne Muscular Dystrophy Drugs Market Shares, by Drug Class (2017A-2023E)
FIG. 15 U.S. Duchenne Muscular Dystrophy Drugs Market, by Therapeutic Approach
FIG. 16 EU5 Duchenne Muscular Dystrophy Drugs Market, by Therapeutic Approach
FIG. 17 Japan Duchenne Muscular Dystrophy Drugs Market, by Therapeutic Approach
FIG. 18 Duchenne Muscular Dystrophy Drugs Market Share, by Company (2017A-2023E)
FIG. 19 Market Trends & Outlook
FIG. 20 Market Driver Relevance Analysis (Current & Future Impact)
FIG. 21 Market Restraint Relevance Analysis (Current & Future Impact)
FIG. 22 SWOT Analysis (Duchenne Muscular Dystrophy Drugs Market)
FIG. 23 Pipeline Assets by Phase
FIG. 24 Exon Skipping and Estimated DMD Risk
FIG. 25 SWOT Analysis (Sarepta Therapeutics)
FIG. 26 SWOT Analysis (PTC Therapeutics)
FIG. 27 SWOT Analysis (Santhera Therapeutics)
FIG. 28 SWOT Analysis (Italfarmaco)
FIG. 29 SWOT Analysis (Catabasis)