Rare Diseases Treatment Market Size, Share & Trends Report

Rare Diseases Treatment Market Size, Share & Trends Analysis Report By Therapeutic Area (Cancer, Musculoskeletal Conditions), By Route Of Administration, By Drug Type, By Distribution Channel, By Region, And Segment Forecasts, 2025 - 2030

  • Report ID: GVR-4-68039-965-6
  • Number of Report Pages: 150
  • Format: PDF, Horizon Databook
  • Historical Range: 2018 - 2024
  • Forecast Period: 2025 - 2030 
  • Industry: Healthcare

Market Segmentation

  • Rare Disease Treatment Therapeutic Area Outlook (Revenue, USD Billion, 2018 - 2030)
    • Cancer
    • Neurological Conditions
    • Cardiovascular Conditions
    • Musculoskeletal Conditions
    • Hematologic Disorders
    • Infectious Diseases
    • Metabolic Disorders
    • Endocrine Disorders
    • Others
  • Rare Disease Treatment Drug Outlook (Revenue, USD Billion, 2018 - 2030)
    • Biologics
    • Biosimilar
    • Small molecules
  • Rare Disease Treatment Route of Administration Outlook (Revenue, USD Billion, 2018 - 2030)
    • Oral
    • Injectable
    • Others
  • Rare Disease Treatment Distribution Channel Outlook (Revenue, USD Billion, 2018 - 2030)
    • Hospital Pharmacy
    • Specialty Pharmacy
    • Online Pharmacy
  • Rare Disease Treatment Regional Outlook (Revenue, USD Billion, 2018 - 2030)
    • North America
      • North America Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
        • Cancer
        • Neurological Conditions
        • Cardiovascular Conditions
        • Musculoskeletal Conditions
        • Hematologic Disorders
        • Infectious Diseases
        • Metabolic Disorders
        • Endocrine Disorders
        • Others
      • North America Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
        • Biologics
        • Biosimilar
        • Small molecules
      • North America Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
        • Oral
        • Injectable
        • Others
      • North America Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
        • Hospital Pharmacy
        • Specialty Pharmacy
        • Online Pharmacy
      • U.S.
        • U.S. Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • U.S. Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • U.S. Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • U.S. Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Canada
        • Canada Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Canada Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Canada Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Canada Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Mexico
        • Mexico Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Mexico Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Mexico Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Mexico Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
    • Europe
      • Europe Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
        • Cancer
        • Neurological Conditions
        • Cardiovascular Conditions
        • Musculoskeletal Conditions
        • Hematologic Disorders
        • Infectious Diseases
        • Metabolic Disorders
        • Endocrine Disorders
        • Others
      • Europe Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
        • Biologics
        • Biosimilar
        • Small molecules
      • Europe Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
        • Oral
        • Injectable
        • Others
      • Europe Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
        • Hospital Pharmacy
        • Specialty Pharmacy
        • Online Pharmacy
      • UK
        • UK Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • UK Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • UK Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • UK Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Germany
        • Germany Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Germany Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Germany Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Germany Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • France
        • France Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • France Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • France Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • France Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Italy
        • Italy Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Italy Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Italy Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Italy Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Spain
        • Spain Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Spain Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Spain Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Spain Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
    • Asia Pacific
      • Asia Pacific Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
        • Cancer
        • Neurological Conditions
        • Cardiovascular Conditions
        • Musculoskeletal Conditions
        • Hematologic Disorders
        • Infectious Diseases
        • Metabolic Disorders
        • Endocrine Disorders
        • Others
      • Asia Pacific Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
        • Biologics
        • Biosimilar
        • Small molecules
      • Asia Pacific Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
        • Oral
        • Injectable
        • Others
      • Asia Pacific Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
        • Hospital Pharmacy
        • Specialty Pharmacy
        • Online Pharmacy
      • Japan
        • Japan Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Japan Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Japan Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Japan Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • China
        • China Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • China Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • China Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • China Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • India
        • India Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • India Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • India Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • India Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Australia
        • Australia Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Australia Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Australia Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Australia Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • South Korea
        • South Korea Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • South Korea Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • South Korea Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • South Korea Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
    • Latin America
      • Latin America Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
        • Cancer
        • Neurological Conditions
        • Cardiovascular Conditions
        • Musculoskeletal Conditions
        • Hematologic Disorders
        • Infectious Diseases
        • Metabolic Disorders
        • Endocrine Disorders
        • Others
      • Latin America Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
        • Biologics
        • Biosimilar
        • Small molecules
      • Latin America Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
        • Oral
        • Injectable
        • Others
      • Latin America Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
        • Hospital Pharmacy
        • Specialty Pharmacy
        • Online Pharmacy
      • Brazil
        • Brazil Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Brazil Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Brazil Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Brazil Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Argentina
        • Argentina Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Argentina Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Argentina Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Argentina Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
    • MEA
      • MEA Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
        • Cancer
        • Neurological Conditions
        • Cardiovascular Conditions
        • Musculoskeletal Conditions
        • Hematologic Disorders
        • Infectious Diseases
        • Metabolic Disorders
        • Endocrine Disorders
        • Others
      • MEA Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
        • Biologics
        • Biosimilar
        • Small molecules
      • MEA Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
        • Oral
        • Injectable
        • Others
      • MEA Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
        • Hospital Pharmacy
        • Specialty Pharmacy
        • Online Pharmacy
      • South Africa
        • South Africa Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • South Africa Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • South Africa Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • South Africa Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Saudi Arabia
        • Saudi Arabia Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Saudi Arabia Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Saudi Arabia Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Saudi Arabia Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • UAE
        • UAE Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • UAE Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • UAE Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • UAE Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy
      • Kuwait
        • Kuwait Rare Disease Treatment Market, By Therapeutic Area 2018 - 2030 (USD Billion)
          • Cancer
          • Neurological Conditions
          • Cardiovascular Conditions
          • Musculoskeletal Conditions
          • Hematologic Disorders
          • Infectious Diseases
          • Metabolic Disorders
          • Endocrine Disorders
          • Others
        • Kuwait Rare Disease Treatment Market, By Drug, 2018 - 2030 (USD Billion)
          • Biologics
          • Biosimilar
          • Small molecules
        • Kuwait Rare Disease Treatment Market, By Route of Administration, 2018 - 2030 (USD Billion)
          • Oral
          • Injectable
          • Others
        • Kuwait Rare Disease Treatment Market, By Distribution Channel, 2018 - 2030 (USD Billion)
          • Hospital Pharmacy
          • Specialty Pharmacy
          • Online Pharmacy

Report content

Qualitative Analysis

  • Industry overview
  • Industry trends
  • Market drivers and restraints
  • Market size
  • Growth prospects
  • Porter’s analysis
  • PESTEL analysis
  • Key market opportunities prioritized
  • Competitive landscape
    • Company overview
    • Financial performance
    • Product benchmarking
    • Latest strategic developments

Quantitative Analysis

  • Market size, estimates, and forecast from 2018 to 2030
  • Market estimates and forecast for product segments up to 2030
  • Regional market size and forecast for product segments up to 2030
  • Market estimates and forecast for application segments up to 2030
  • Regional market size and forecast for application segments up to 2030
  • Company financial performance
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